Physician Education Series: Spinal Muscular Atrophy - A Success Story for Gene Therapy

Presented by Isabella Herman, M.D., Ph.D.

This presentation will offer an overview of the symptoms and types of spinal muscular atrophy and introduce the concept of gene therapy. It will also discuss the treatment landscape for spinal muscular atrophy.

About Physician Education Series

The Physician Education Series is a series of free CME accredited medical and clinical presentations covering various aspects of pediatric specialties, including screenings, diagnosis and treatments, co-occuring condition and differential diagnosis. The one-hour presentations are presented by medical, clinical and research staff at Boys Town National Research Hospital.

Presentations are free and include AMA Category 1 Credit.